Loading Events

« All Events

  • This event has passed.

The Duchenne Platform Trial Stakeholder Meeting

September 9, 2019

The Duchenne Platform Trial is being designed to increase access to therapeutic trials across the Duchenne community, with the goals of:

  • More rapid completion of testing and approval of new DMD therapies
  • Reduced clinical trial start-up and execution time
  • Enhanced patient experience, reduced number on placebo
  • Potential for rapidly testing combination therapies
  • The trial will study multiple drugs in multiple patient types with one common placebo-controlled arm.

    The stakeholder meeting will be hosted by I-ACT for Children, Parent Project Muscular Dystrophy and the Critical Path Institute.

    More details to come shortly!


September 9, 2019