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The Duchenne Platform Trial Stakeholder Meeting

September 9, 2019

The Duchenne Platform Trial is being designed to increase access to therapeutic trials across the Duchenne community, with the goals of:

  • More rapid completion of testing and approval of new DMD therapies
  • Reduced clinical trial start-up and execution time
  • Enhanced patient experience, reduced number on placebo
  • Potential for rapidly testing combination therapies
  • The trial will study multiple drugs in multiple patient types with one common placebo-controlled arm.

    The stakeholder meeting will be hosted by I-ACT for Children, Parent Project Muscular Dystrophy and the Critical Path Institute.

    More details to come shortly!

Details

Date:
September 9, 2019