News and Events

I-ACT FOR CHILDREN TO CO-HOST DUCHENNE MUSCULAR DYSTROPHY PLATFORM TRIAL STAKEHOLDER MEETING

SHERATON SILVER SPRING | SILVER SPRING, MD
SEPTEMBER 9, 2019 | 8:30 AM-4:30 PM

I-ACT for Children will co-host the first Duchenne Muscular Dystrophy Platform Trial Community Meeting on Sept. 9 with collaborators Parent Project Muscular Dystrophy and the Critical Path Institute.

The Duchenne Platform Trial is being designed to increase access to therapeutic trials for the Duchenne community, with the goals of:

  • More rapid completion of testing and approval of new Duchenne therapies
  • Reduced clinical trial start-up and execution time
  • Enhanced patient experience, reduced number on placebo
  • Potential for rapidly testing combination therapies

The meeting will be an opportunity for stakeholders to provide input into the design of the platform trial and gain consensus on critical design elements.

Registration for the in-person meeting has closed, but the meeting will be live-streamed for those unable to attend in-person. Click below to register for the live-stream:

 

 

 

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